Are you a Carrier?
National Human Genome Research Institute (NHGRI) has completed Phase 1 of its clinical trial of ManNac.
National Human Genome Research Institute (NHGRI) is recruiting patients for a Natural History Study of patients with HIBM. MORE INFO
Hereditary Inclusion Body Myopathy-Disease Monitoring (HIBM-DMP): A Combined Registry and Prospective Observational Natural History Study to Assess HIBM Disease. MORE INFO
NDF Appoints new Lale Welsh as new Executive Director - PRESS RELEASE
NDF proud sponsor of "Rare Disease Day Symposium" - See Videos
Results from Ultragenyx Pharmaceutical’s Phase 1 study of UX001. MORE INFO